Target group

SMA patients who want to register must either have already been genetically tested or have a genetic test coming up soon. This is necessary so that we can make sure the patient has the right genetic diagnosis for a particular trial or that any other information we give them is relevant to their condition.

On the TREAT-NMD website, you can find a list of registries in other countries where you might find the right registry to sign up if you are not resident in the UK or in Ireland. Information about DMD/BMD (Duchenne/Becker muscular dystrophy) registries in various countries and about registries for (other) rare inherited muscular disorders can also be found there.